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Status: Closed — this petition is no longer accepting signatures.

Lacking FDA approval for α- thalassemia Gene therapies

Lacking FDA approval for α- thalassemia Gene therapies

Closed — 15 supporters Verified

Final supporters

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Someone
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Kimberly G.
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Sanya D.
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Team C.
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Team C.
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Someone
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Pari B.
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Mehul M.
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Someone
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Julia S.
+5 more
MF
Started by Mustafa Farooq 8 years, 6 months ago

α-thalassemia is one of the most prevalent genetic disorders in the Eastern hemisphere. In the past, successful forms of therapy have been extremely difficult to identify. However, with recent developments in gene therapy many forms of treatment have been discovered. These forms of treatment are quite vital to the survival of many individuals suffering from thalassemia, yet lack of FDA approval has thwarted them from being accessible to the modern medical field and practices. Sign below if you would like to have your voice heard.

6 Comments

A
Anonymous
8 years ago Featured

Guidelines for trials of genetic therapy should better balance the genuine concerns about patient safety and the requirements for extensive testing for each unique variant of a general therapy.

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Sarah Kim
8 years ago Featured

my nephew has this and watching him go through transfusions is heartbreaking. why is the fda dragging their feet on this when lives are literally at stake?

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Jonny Appleseed
8 years ago

Nice job guys!

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Team Copper
8 years ago

Nice job guys!

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Mehul Mehra
8 years ago

Yeah!

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Giselle
8 years ago

:)